Neurodegenerative

Sangamo Secures $50M Upfront in Neurodegenerative Pact with Roche’s Genentech

9 months ago talkbio0Tagged biobucks, genentech, milestone payments, Neurodegenerative, Roche (company), Sangamo

Sangamo, Roche, Genentech, neurodegenerative, biotech, licensing deal, milestone payments, biobucks

BioMarin’s Brineura Receives Significant Label Expansion from FDA for Children Under 3 with CLN2 Disease

9 months ago talkbio0Tagged Alfa, BioMarin, Brineura, cerliponase, Child, Deterioration, expansion, Injection of therapeutic agent, Intraventricular, Labels (device), motor ability, Neurodegenerative, Symptoms aspect, TPP1 gene, United States Food and Drug Administration

BioMarin, Brineura, FDA, Label Expansion, CLN2 Disease, Children Under 3, Cerliponase Alfa, Intraventricular Injection, Motor Ability Deterioration, Neurodegenerative Symptoms

FDA’s Operation Warp Speed for Rare Diseases: First Five Participants Announced

11 months ago talkbio0Tagged Beginning, conditions, gene therapy, Neurodegenerative, Operative Surgical Procedures, Programs - Publication Format, United States Food and Drug Administration, Warp Speed

FDA, Operation Warp Speed, Rare Diseases, START Program, Gene Therapies, Neurodegenerative Conditions