Pauses
FDA Official Says Sarepta Faces Major Hurdles to Reintroduce DMD Therapy Elevidys
Sarepta; Elevidys; FDA; Duchenne muscular dystrophy; gene therapy; CBER; safety concerns; shipment pause; new studies; approval status
Sarepta, bowing to FDA pressure, pauses shipments of Duchenne gene therapy Elevidys
Sarepta Therapeutics; FDA; Elevidys; Duchenne muscular dystrophy; gene therapy; shipment pause; patient deaths; safety concerns
Pharma stocks swerve as Trump hits pause on most tariffs
Market, Transplant Registry Unified Management Program, Pauses