Spinal Muscular Atrophy – Page 2

Scholar Rock’s Apitegromab Shows Significant Improvement in Spinal Muscular Atrophy Treatment

11 months ago talkbio0Tagged apitegromab, Clinical Trials, GDF8 protein, human, Improvement, Motor function (observable entity), Phase 3, Psychological inhibition, Spinal Muscular Atrophy

Spinal Muscular Atrophy (SMA), Apitegromab, Phase 3 Clinical Trial, Motor Function Improvement, Myostatin Inhibition

Voyager Therapeutics Secures $100M Upfront Payment in Expanded Gene Therapy Partnership with Novartis

12 months ago talkbio0Tagged Biotechnology, capsid discovery, gene therapy, Huntington Disease, Novartis, Spinal Muscular Atrophy, Tracer

Gene therapy, Novartis, Voyager Therapeutics, Huntington’s disease, Spinal muscular atrophy (SMA), TRACER capsid discovery platform, Biotechnology collaboration

Biogen Announces Positive Results from Higher Dose Spinraza Study in Spinal Muscular Atrophy Patients

12 months ago talkbio0Tagged Biogen, Clinical Research, Clinical Trials, DEVOTE, Dosage, High, Spinal Muscular Atrophy, Spinraza

Biogen, Spinraza, spinal muscular atrophy, SMA, higher dose, clinical trial, DEVOTE study