gene therapy – Page 8

Biopharma Companies uniQure and Arbutus Announce Workforce Reductions to Focus on Priority Programs

9 months ago talkbio0Tagged Arbutus Biopharma, Biopharma, Clinical Trials, gene therapy, Priority, UniQure

uniQure, Arbutus Biopharma, layoffs, workforce reduction, biopharma, priority programs, gene therapy, clinical trials

Sanofi Sues Sarepta Over US Patents for Gene Therapy Treatments

9 months ago talkbio0Tagged Duchenne, ELEVIDYS, gene therapy, Legal patent, Muscular Dystrophy, sanofi

Sanofi, Sarepta, Gene Therapy, Patents, Elevidys, Duchenne Muscular Dystrophy

Pfizer Lays Off 210 Workers in North Carolina Following Discontinuation of Duchenne Gene Therapy

9 months ago talkbio0Tagged Duchenne Gene Therapy, gene therapy, layoffs, Muscular Dystrophy, North Carolina, Pfizer

Pfizer, Layoffs, North Carolina, Duchenne Gene Therapy, Muscular Dystrophy, Gene Therapy Program

Pfizer and Sangamo’s Gene Therapy Shows Superiority Over Prophylaxis in Hemophilia A Study

9 months ago talkbio0Tagged factor VIII, gene therapy, Giroctocogene fitelparvovec, Hemophilia A, Hemorrhage, Pfizer, prevention & control, Rating (action), Sangamo

Pfizer, Sangamo, gene therapy, hemophilia A, prophylaxis, giroctocogene fitelparvovec, bleeding rate, Factor VIII

Pfizer’s Hemophilia A Gene Therapy Candidate Achieves Phase 3 Success

9 months ago talkbio0Tagged Fitelparvovec, gene therapy, Giroctocogene, Hemophilia A, Hemorrhage, Pfizer, Phase 3 trial, Rating (action)

Pfizer, Hemophilia A, Gene Therapy, Phase 3 Trial, Giroctocogene Fitelparvovec, Bleeding Rate Reduction

Bluebird Bio’s Fertility Support Program for Gene Therapies Rejected by HHS Inspector General

9 months ago talkbio0Tagged Anti-Kickback Rules, CHARGE Syndrome, Family Turdidae (organism), Fertility, gene therapy, Generalized, Inspector, Skysona, Support, device

Bluebird Bio, Gene Therapy, Fertility Support, HHS Inspector General, Zynteglo, Skysona, Anti-Kickback Rules

4DMT’s Wet AMD Gene Therapy Results Disappoint Investors, Stock Plummets

9 months ago talkbio0Tagged Clinical Trials, gene therapy, Glycogen storage disease type II, Stock Performance

4DMT, Wet AMD, Gene Therapy, Stock Performance, Clinical Trials

Vertex Pharmaceuticals Sues US Government Over Fertility Assistance Program for Gene Therapy Patients

9 months ago talkbio0Tagged Biologic Preservation, Fertility, gene therapy, Government, Health Insurance

Vertex Pharmaceuticals, gene therapy, fertility assistance program, lawsuit, US government, health insurance, fertility preservation

Lexeo Therapeutics Reports Promising Early Data for Gene Therapy LX2006 in Friedreich Ataxia Cardiomyopathy

9 months ago talkbio0Tagged Ataxia, Cardiomyopathies, Clinical Trials, gene therapy, Hereditary Diseases, Infrequent, Lexeo, LX2006

Lexeo Therapeutics, LX2006, Gene Therapy, Friedreich Ataxia, Cardiomyopathy, Clinical Trials, Rare Genetic Disorders

uniQure Announces Positive Interim Data Update Demonstrating Slowing of Disease Progression in Phase I/II Trials of AMT-130 for Huntington’s Disease

10 months ago talkbio0Tagged AMT-130, cUHDRS, Disease Progression, gene therapy, Huntington 's disease, Huntington 's Disease Rating Scale, Identifier, neurofilament protein L, NfL, Phase I/II trials, Regenerative Medicine, RMAT, Unified - Type of Agreement, UniQure

uniQure, Huntington’s disease, AMT-130, gene therapy, Phase I/II trials, disease progression, neurofilament light protein (NfL), Unified Huntington’s Disease Rating Scale (cUHDRS), Regenerative Medicine Advanced Therapy (RMAT) designation