gene therapy – Page 20

Controversy Surrounds FDA’s Fast-Track Approval of Sarepta’s Duchenne Muscular Dystrophy Gene Therapy

2 years ago talkbio0Tagged Accelerated, Advocacy, Approved, Clinical Trials, DMD, Duchenne, Effectiveness, gene therapy, Muscular Dystrophy, Muscular Dystrophy, Duchenne, Regulation of biological process, Safety, United States Food and Drug Administration

FDA, Sarepta Therapeutics, Duchenne Muscular Dystrophy (DMD), gene therapy, accelerated approval, controversy, clinical trials, efficacy, safety, patient advocacy, regulatory process.

Pfizer’s Revolutionary Hemophilia B Gene Therapy Gains FDA Approval and Introduces Unique Warranty Program

2 years ago talkbio0Tagged Approved, Biotechnology, Blood coagulation, gene therapy, Health care facility, Hemophilia B, Hereditary Diseases, Pfizer, United States Food and Drug Administration

Pfizer, FDA, Hemophilia B, Gene Therapy, Approval, Warranty, Treatment, Genetic Disorder, Blood Clotting, Healthcare, Biotechnology

FDA Approves Pfizer’s Hemophilia B Gene Therapy with a $3.5 Million Price Tag

2 years ago talkbio0Tagged Approved, Biotechnology, Financial cost, gene therapy, Health care facility, Hemophilia B, Hereditary Diseases, Pfizer, Pricing, United States Food and Drug Administration

Pfizer, FDA, hemophilia B, gene therapy, approval, pricing, healthcare, biotechnology, rare diseases, genetic disorders, treatment cost.