Temporal Concept
Sanofi’s Amlitelimab Shows Mixed Phase 3 Results in Eczema Trials, Clouds Blockbuster Hopes but Advances to Regulatory Filings
Sanofi; amlitelimab; Phase 3; eczema; atopic dermatitis; COAST; SHORE; vIGA-AD; EASI-75
Orphan Drug Trends: A Data-Driven Analysis
orphan drugs; market growth; rare diseases; FDA approvals; genomics; reimbursement challenges
IntraBio’s Levacetylleucine Succeeds in Phase 3 Trial for Ataxia-Telangiectasia, Plans FDA and EMA Approval
IntraBio; levacetylleucine; Ataxia-Telangiectasia; Phase 3; FDA approval; EMA; rare disease
Court Rejects HHS Motion to Dismiss Lawsuit Over US Childhood Vaccine Overhaul as Clinician Groups Push Forward
childhood vaccine overhaul; HHS; lawsuit; ACIP; AAP; CDC; RFK Jr.; immunization schedule
Exciva Raises $59M Series B to Fund Phase 2 Trial of Deraphan for Alzheimer’s Agitation
Exciva; Series B; $59M; Alzheimer’s; agitation; Deraphan; Phase 2; neuropsychiatry
Corvus Pharmaceuticals Reports Positive Phase 1 Data for Soquelitinib in Atopic Dermatitis, Exceeding Expectations
Corvus Pharmaceuticals; soquelitinib; Phase 1; atopic dermatitis; EASI reduction; ITK inhibitor
Nxera Pharma Reports Positive Phase 3 Results for Daridorexant in South Korea Insomnia Trial
Nxera Pharma; daridorexant; Phase 3; insomnia; South Korea; QUVIVIQ
Genmab and AbbVie’s Epcoritamab Misses Overall Survival Endpoint but Meets PFS in Phase 3 DLBCL Trial
Genmab; AbbVie; epcoritamab; Epkinly; EPCORE DLBCL-1; Phase 3; DLBCL; lymphoma; overall survival; progression-free survival
J&J Reports Positive Phase 3 MajesTEC-9 Results for Tecvayli in Earlier Multiple Myeloma
Tecvayli; J&J; Phase 3; MajesTEC-9; multiple myeloma; PFS; OS
Veradermics Files for $100 Million IPO to Advance Oral Minoxidil Hair Loss Treatment
Veradermics; IPO; hair loss; minoxidil; VDPHL01; Phase 3