SpringWorks Therapeutics Secures FDA Approval for Gomekli to Treat NF1-Related Tumors

SpringWorks Therapeutics, Gomekli, mirdametinib, FDA approval, neurofibromatosis type 1 (NF1), plexiform neurofibromas (PN), rare disease treatment, MEK inhibitor

Voyager Therapeutics Halts ALS Gene Therapy Development Due to Off-Target Effects

SOD1 ALS gene therapy, Off-target effects, VY9323, siRNA payload, TRACER capsid, Preclinical data, Drug development delay