October 2024
Poseida Therapeutics Advances Non-Viral Gene Editing Therapy for Hereditary Angioedema
Poseida Therapeutics, non-viral gene editing, hereditary angioedema (HAE), P-KLKB1-101, Cas-CLOVER, liver-directed gene therapy
Marinus Pharmaceuticals to Reduce Workforce and Explore Strategic Alternatives Following Disappointing Trial Results
Marinus Pharmaceuticals, workforce reduction, strategic alternatives, Ztalmy trial, pharmaceutical industry, biotech layoffs
Thermo Fisher Forecasts Revenue Growth in 2025 Amid Easing Market Challenges
Thermo Fisher Scientific, revenue forecast, 2025 growth, easing headwinds, biotech funding, pharmaceutical sector, laboratory products, analytical instruments.
Roche CEO Urges Antitrust Regulators to Block Novo Holdings’ Acquisition of Catalent
Novo Holdings, Catalent, Roche, Antitrust Regulators, Pharmaceutical Industry, Mergers and Acquisitions
Roche Revisits Dyno for AAV Technology with $50M Upfront Payment
Roche, Dyno Therapeutics, AAV technology, gene therapy, neurological diseases, strategic partnership
Pfizer Announces Additional Layoffs in North Carolina Following DMD Trial Setback
Pfizer layoffs, North Carolina, Duchenne muscular dystrophy (DMD), gene therapy trial failure, cost-cutting measures
Ocuphire Pharma Acquires Opus Genetics, Expanding into Inherited Retinal Disease Gene Therapies
Ocuphire Pharma, Opus Genetics, gene therapy, inherited retinal diseases (IRDs), merger, acquisition, biopharmaceutical, ophthalmic treatments
Alpha-9 Radios Secures $175M Funding for RLT Portfolio Advancement
Alpha-9 radios, $175M funding, RLT portfolio, radiopharmaceuticals, biotech investment
Vabysmo’s Growth Pace Slows in Q3, Still on Track for Dominance in Eye Disease Market
Vabysmo, Roche, Regeneron, Eylea HD, eye disease market, vascular endothelial growth factor A (VEGF-A) therapy, age-related macular degeneration (AMD), diabetic macular edema (DME).
NICE Rejects Alzheimer’s Drug Kisunla Despite UK Regulatory Approval
NICE, Alzheimer’s disease, donanemab, Kisunla, Eli Lilly, MHRA, NHS, cost-effectiveness